Pink Sheet is part of Informa PLC

This site is operated by a business or businesses owned by Informa PLC and all copyright resides with them. Informa PLC’s registered office is 5 Howick Place, London SW1P 1WG. Registered in England and Wales. Number 8860726.

This copy is for your personal, non-commercial use. For high-quality copies or electronic reprints for distribution to colleagues or customers, please call +44 (0) 20 3377 3183

Printed By

UsernamePublicRestriction

CSL Behring's Corifact Clears FDA On 14-Patient Trial

This article was originally published in The Pink Sheet Daily

Executive Summary

The orphan drug, for a rare blood disorder, is the latest in a history of drugs for ultra-orphan conditions.

You may also be interested in...



Orphan Drugs Need Easier, Speedier Approval, Not More Exclusivity, CEO Says

Advocates and drug developers continue to call for an Orphan Drug Act renovation – not to add more years of marketing exclusivity, but to consider allowing easier and cheaper development programs.

Orphan Drugs Need Easier, Speedier Approval, Not More Exclusivity, CEO Says

Advocates and drug developers continue to call for an Orphan Drug Act renovation – not to add more years of marketing exclusivity, but to consider allowing easier and cheaper development programs.

Orphan Drug Safety: FDA Asks How Much Pre-Approval Data Is Enough?

Agency's Advisory Committee for Pharmaceutical Science and Clinical Pharmacology will be asked to weigh pre-approval data requirements and discuss innovative approaches to boosting drug development for rare diseases at its March 2 meeting.

Related Content

Topics

UsernamePublicRestriction

Register

PS071843

Ask The Analyst

Ask the Analyst is free for subscribers.  Submit your question and one of our analysts will be in touch.

Your question has been successfully sent to the email address below and we will get back as soon as possible. my@email.address.

All fields are required.

Please make sure all fields are completed.

Please make sure you have filled out all fields

Please make sure you have filled out all fields

Please enter a valid e-mail address

Please enter a valid Phone Number

Ask your question to our analysts

Cancel