BIO 2019 Notebook: Sharpless On Pricing, Marks On Gene Therapy, Takeda On M&A
Executive Summary
News and views from day two of the BIO International Convention: US FDA's Sharpless decries the focus on the price of "medical miracle" Zolgensma; CBER Director Marks talks about how his division will staff up to review cell and gene therapy candidates; and Takeda explains why its business development philosophy leads to the valuation seen in the Ariad buyout.
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