EU's CHMP Clears Europe's First Gene Therapy, UniQure's Glybera
This article was originally published in The Pink Sheet Daily
Executive Summary
After three previous negative votes, the Netherlands biotech uniQure gains the first positive opinion from the Committee for Medicinal Products for Human Use for a gene therapy in Europe. Glybera is used to treat the ultra-rare condition lipoprotein lipase deficiency.
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