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BioCryst & Celgene Suffer English Funding Setback For Rare Disease Drugs

NICE’s Recommendations Are Out For Consultation until 28 July

Executive Summary

Orladeyo and Inrebic have been approved in Great Britain but they will not be available under the National Health Service unless their manufacturers can convince the health technology assessment body, NICE, that their products are cost-effective.

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New Sickle Cell Treatment & Ten Other Drugs Win English Funding Approval

Health technology assessment body NICE has also issued guidances rejecting three products.

UK Early Access For BioCryst’s Hereditary Angioedema Drug

The HAE product, which meets the four criteria for pre-licensing use under the UK’s early access scheme, is currently undergoing regulatory evaluation in the EU, the US and Japan, with approval decisions expected in the last two countries next month.

COVID-19 Treatment Xevudy Wins UK Approval; Preclinical Data Shows Promise Against Omicron

New developments on the COVID-19 front also include the European Medicines Agency starting a rolling review of Valneva’s investigational COVID-19 vaccine, and the UK government signing contracts with Pfizer/BioNTech and Moderna to buy more doses of their vaccines.


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