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United Kingdom Rare Diseases Regulation

UK Allows Early Access To Alnylam’s Lumasiran For Ultra-Rare Disorder

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Executive Summary

UK patients diagnosed with primary hyperoxaluria Type 1 can now be prescribed lumasiran, which is still being reviewed for EU-wide approval. Patients in the US, Germany and other EU countries can also get the drug under early access schemes.

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This copy is for your personal, non-commercial use. For high-quality copies or electronic reprints for distribution to colleagues or customers, please call +44 (0) 20 3377 3183

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