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BioMarin Kills Kyndrisa, But Duchenne Pursuit Not Over

This article was originally published in The Pink Sheet Daily

Executive Summary

Seeing no clear path to approval in the US or Europe for its muscular dystrophy drug drisapersen, BioMarin shelves it , plus three first-generation follow-on products. But it continues to "explore" its early stage next-generation oligonucleotides as potential treatments for DMD.


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