Pink Sheet is part of the Business Intelligence Division of Informa PLC

This site is operated by a business or businesses owned by Informa PLC and all copyright resides with them. Informa PLC’s registered office is 5 Howick Place, London SW1P 1WG. Registered in England and Wales. Number 8860726.

This copy is for your personal, non-commercial use. For high-quality copies or electronic reprints for distribution to colleagues or customers, please call +44 (0) 20 3377 3183

Printed By


Cystic Fibrosis Market Snapshot: Disease-Modifying Drugs Elusive 24 Years After Discovery Of Root Cause

Executive Summary

The discovery in 1989 of the underlying genetics causing cystic fibrosis was expected to spur broad development of disease-modifying therapies. As of 2013, however, only one such drug is on the market, for a small subset of CF patients, and a few other candidates are in clinical development.


Related Content

Beyond Orkambi: Cystic Fibrosis Pipeline Includes Other Genetic, Symptomatic Therapy Approaches
Corbus Believes A Different Inflammation-Fighting Approach Will Serve All CF Patients
U.K.’s Verona Explores Cystic Fibrosis Role For Novel Bronchodilator
PTC Adds To Management Team In Sign Of Progress Beyond Setbacks
Uncertain About HCV, Vertex Doubles Down On CF, Looks To Sell Off Pipeline Assets
Bronchitol AdComm Shows Difficulty Of Following In Kalydeco’s Shadow
Deals of the Week: Sanofi-Pasteur/CureVac, Shire/Shionogi, Genzyme/CFF, Medicis/Graceway
Not The Way You Want To Start Your Year: Inspire Cystic Fibrosis Drug Fails Late
Pfizer Adds To Specialty Care Division With Purchase Of FoldRx
Breath Of Fresh Air For Cystic Fibrosis Drug Pipeline


Related Companies

Related Deals




Ask The Analyst

Please Note: You can also Click below Link for Ask the Analyst
Ask The Analyst

Your question has been successfully sent to the email address below and we will get back as soon as possible. my@email.address.

All fields are required.

Please make sure all fields are completed.

Please make sure you have filled out all fields

Please make sure you have filled out all fields

Please enter a valid e-mail address

Please enter a valid Phone Number

Ask your question to our analysts