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PTC Fully Enrolls Duchenne MD Trial; Expects Top-Line Data In Early 2010

This article was originally published in Pharmaceutical Approvals Monthly

Executive Summary

Despite targeting an indication with a very small population, PTC Therapeutics has fully enrolled a pivotal trial for ataluren (PTC124), its potential disease-modifying therapy for Duchenne muscular dystrophy, and expects to produce top-line data early next year. Regulatory filings in the U.S. and EU could follow closely if the data are promising

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